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genetic diseases

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“I Can’t Tell You How Many Times People Said ‘It Will Never Work’”: The Pioneers Of Gene Therapy Honored In Two Of This Year’s Breakthrough Prizesillustration of two scientists cutting and adding in new bits of DNA to represent gene editing and gene therapy

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“I Can’t Tell You How Many Times People Said ‘It Will Never Work’”: The Pioneers Of Gene Therapy Honored In Two Of This Year’s Breakthrough Prizesillustration of two scientists cutting and adding in new bits of DNA to represent gene editing and gene therapy
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health-iconmedicine

“I Can’t Tell You How Many Times People Said ‘It Will Never Work’”: The Pioneers Of Gene Therapy Honored In Two Of This Year’s Breakthrough Prizes

clock-iconApril 27, 2026

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First-Of-Its-Kind Gene Therapy For Inherited Hearing Loss Approved By FDA As Trial Shows Improvement In 80 Percent Of Patientsillustration of DNA on a purple background

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First-Of-Its-Kind Gene Therapy For Inherited Hearing Loss Approved By FDA As Trial Shows Improvement In 80 Percent Of Patientsillustration of DNA on a purple background
health-iconmedicine

First-Of-Its-Kind Gene Therapy For Inherited Hearing Loss Approved By FDA As Trial Shows Improvement In 80 Percent Of Patients

clock-iconApril 24, 2026

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World-First Gene Therapy Improves Vision For Man With Rare, Previously Untreatable Form Of Blindnessdiagonal line of hexagonal wooden tiles on a bright blue background; each tile contains an image of a helix to represent DNA. In the middle of the line, a red tile is being replaced with a green one.

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World-First Gene Therapy Improves Vision For Man With Rare, Previously Untreatable Form Of Blindnessdiagonal line of hexagonal wooden tiles on a bright blue background; each tile contains an image of a helix to represent DNA. In the middle of the line, a red tile is being replaced with a green one.
health-iconmedicine

World-First Gene Therapy Improves Vision For Man With Rare, Previously Untreatable Form Of Blindness

clock-iconAugust 4, 2025
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Newly Discovered Cell Structure Might Hold Key To Understanding Devastating Genetic DisordersEight images of the newly discovered organelle

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Newly Discovered Cell Structure Might Hold Key To Understanding Devastating Genetic DisordersEight images of the newly discovered organelle
health-iconhealth

Newly Discovered Cell Structure Might Hold Key To Understanding Devastating Genetic Disorders

clock-iconJune 30, 2025
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Infant Becomes First Human Ever To Receive Personalized CRISPR Gene Therapy TreatmentDrs. Kiran Musunuru and Rebecca Ahrens-Nicklas with patient KJ.

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Infant Becomes First Human Ever To Receive Personalized CRISPR Gene Therapy TreatmentDrs. Kiran Musunuru and Rebecca Ahrens-Nicklas with patient KJ.
health-icongenetics

Infant Becomes First Human Ever To Receive Personalized CRISPR Gene Therapy Treatment

clock-iconMay 16, 2025
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Rare Genetic Motor Neuron Disease Treated In Womb For The First Time Close up of woman expecting baby having appointment with doctor, her hands are holding the baby bump

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Rare Genetic Motor Neuron Disease Treated In Womb For The First Time Close up of woman expecting baby having appointment with doctor, her hands are holding the baby bump
health-iconmedicine

Rare Genetic Motor Neuron Disease Treated In Womb For The First Time

clock-iconFebruary 24, 2025
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What Is The “Celtic Curse” And Could You Be At Risk?Celtic cross headstone against backdrop of green fields, with circular inlay on the right showing red blood cells and DNA double helix

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What Is The “Celtic Curse” And Could You Be At Risk?Celtic cross headstone against backdrop of green fields, with circular inlay on the right showing red blood cells and DNA double helix
health-iconhealth

What Is The “Celtic Curse” And Could You Be At Risk?

clock-iconJanuary 18, 2024
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Discovery Of 60 New Genetic Diseases Finally Brings Answers For Thousands Of Childrenmagnifying glass zooms in on DNA molecule on background of multicolored stripes to represent sequencing data

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Discovery Of 60 New Genetic Diseases Finally Brings Answers For Thousands Of Childrenmagnifying glass zooms in on DNA molecule on background of multicolored stripes to represent sequencing data
health-iconmedicine

Discovery Of 60 New Genetic Diseases Finally Brings Answers For Thousands Of Children

clock-iconApril 14, 2023
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19-Month-Old Treated For Deadly Genetic Condition With World’s Most Expensive Drugbrain with dna strand

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19-Month-Old Treated For Deadly Genetic Condition With World’s Most Expensive Drugbrain with dna strand
health-iconmedicine

19-Month-Old Treated For Deadly Genetic Condition With World’s Most Expensive Drug

clock-iconFebruary 15, 2023
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First-Of-Its-Kind Study Reveals How Many Americans Have Mysterious VEXAS Syndromeman giving blood

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First-Of-Its-Kind Study Reveals How Many Americans Have Mysterious VEXAS Syndromeman giving blood
health-iconHealth and Medicine

First-Of-Its-Kind Study Reveals How Many Americans Have Mysterious VEXAS Syndrome

clock-iconJanuary 24, 2023
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For First Time Ever, Rare Genetic Disorder Is Treated In The WombAyla Bashir

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For First Time Ever, Rare Genetic Disorder Is Treated In The WombAyla Bashir
health-iconmedicine

For First Time Ever, Rare Genetic Disorder Is Treated In The Womb

clock-iconNovember 10, 2022
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“Is Curing Patients A Sustainable Business Model?,” Asks Goldman Sachs Report In 2018article image

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“Is Curing Patients A Sustainable Business Model?,” Asks Goldman Sachs Report In 2018article image
health-iconHealth and Medicine

“Is Curing Patients A Sustainable Business Model?,” Asks Goldman Sachs Report In 2018

clock-iconApril 16, 2018
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Gene Therapy For Rare Forms Of Blindness Will Cost Nearly Half A Million Per Eyearticle image

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Gene Therapy For Rare Forms Of Blindness Will Cost Nearly Half A Million Per Eyearticle image
health-iconHealth and Medicine

Gene Therapy For Rare Forms Of Blindness Will Cost Nearly Half A Million Per Eye

clock-iconJanuary 4, 2018